BioMarin Pharmaceutical Inc.  

Novato,  CA 
United States
https://www.biomarin.com
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Welcome to the BioMarin Global Medical Information Booth.

Profile

BioMarin is a world leader in developing and commercializing innovative therapies for rare diseases driven by genetic causes. With a 20-year history, BioMarin remains steadfast to its original mission - to bring new treatments to market that will make a big impact on small patient populations. These conditions are often inherited, difficult to diagnose, progressively debilitating, have few, if any, treatment options, and are usually ignored.  Visit www.biomarin.com to learn more.


 Products

  • Global Medical Information Virtual Booth
    For full prescribing information, including boxed warnings for PALYNZIQ® (pegvaliase-pqpz) and VIMIZIM® (elosulfase alfa), please see full prescribing information available at the product websites listed below....

  • See Enlarged Marketed And Pipeline Panel

    Our Marketed Programs Include:

    PALYNZIQ® (pegvaliase-pqpz) Injection self-administered enzyme substitution therapy for PKU

    Additional information is available at: https://www.palynziq.com/
    BRINEURA® (cerliponase alfa) for CLN2 Disease

    Additional information is available at: https://www.brineura.com/
    VIMIZIM® (elosulfase alfa) for MPS IVA

    Additional information is available at: https://www.vimizim.com/
    KUVAN® (sapropterin dihydrochloride) Tablets for Oral Use and Powder for Oral Solution for PKU

    Additional information is available at: https://www.kuvan.com/
    NAGLAZYME® (galsulfase) for MPS VI

    Additional information is available at: https://www.naglazyme.com/


    Our Investigational Programs Include:

    Vosoritide (BMN 111): Analog of CNP for Achondroplasia

    Valoctocogene Roxaparvovec (BMN 270): AAV-Gene Therapy for Hemophilia A

    BMN 307: AAV-Gene Therapy for Phenylketonuria (PKU)

    BMN 331: AAV-Gene Therapy for Hereditary Angioedema (HAE)

    DiNA-001: AAV-Gene Therapy for Hypertrophic Cardiomyopathy (HCM)

     

    If you have any questions regarding our marketed or investigational programs, please contact BioMarin Global Medical Information by submitting a request via our web request form located here: Web Request Form