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    Sponsors

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    Amicus Therapeutics

    Amicus Therapeutics

    Acadia Pharma

    Acadia Pharma

    Rhthym Pharma

    Rhthym Pharma

    Oxford Nanopore

    Oxford Nanopore

    Sarepta Therapeutics

    Sarepta Therapeutics

    Mirum Pharmaceuticals

    Mirum Pharmaceuticals

    PTC Therapeutics

    PTC Therapeutics

    Ambry Genetics

    Ambry Genetics

    UCB

    UCB

    Inozyme Pharma

    Inozyme Pharma

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    One West Pratt Street
    Baltimore, MD 21201-2499
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